CheckRare
Rare Diseases Are Our Focus, Expertise, and Passion.
CheckRare is a learning platform for healthcare professionals and the rare disease community. We provide expert discussions regarding rare diseases, current and emerging therapies, clinical trials, advocacy, and BioPharma companies.
Riliprubart for the Treatment of CIDP
Linvoseltamab Combination Therapy in Patients With Relapsed/Refractory Multiple Myeloma
Phase 3 GLISTEN Trial in Patients With Primary Biliary Cholangitis
Evaluating Nerandomilast in Patients With Rare Pulmonary Fibrotic Conditions
Evolving Policy Landscapes for Rare Disease Access
Genetic Testing for WHIM Syndrome
Linerixibat Reduces Itching in Patients with PBC
Current Challenges Facing the ALS and FTD Communities
Diagnostic Odyssey With Histiocytosis
Patient Advocacy in CACNA1A-Related Disorders
Disease Severity and Progression in Patients With ENPP1 Deficiency
The Current Landscape of SYNGAP1-Related Disorders
The Role of Mental Health in Rare Disease Patient Outcomes
Patient Experience With Stevens-Johnson Syndrome
Accelerated Approval Treatment for Patients With Amyotrophic Lateral Sclerosis
A Family’s Experience With ALSP
Advice for Patients With Sickle Cell Anemia
The Undiagnosed Disease Network
Phase 3 Studies Lead to Approval of Fitusiran for Hemophilia A and B
Repurposing Shelved Assets for Rare Diseases
Ethical Concerns in Rare Diseases and Expanded Access Programs
The Diversity of Patient Advocacy Group Initiatives
CAMP4 Therapeutics’ Programs For Urea Cycle Disorders and SYNGAP1
A Patient’s Diagnostic Journey With Idiopathic Pulmonary Hemosiderosis (IPH)
Navigating the Challenges of the Orphan Drug Market
Newly Approved Treatment Targets Underlying Cause of IgG4-Related Disease
Mental Health and the Rare Disease Community
Urea Cycle Disorders: Overview and Developing Novel Therapies
Positive Safety and Efficacy Data for Intrathecal Administration of Gene Therapy for SMA
Challenges Faced by Rare Disease Patients in India