Gene (and transcript) directed precision therapeutics for rare neuromuscular disease of childhood: From GAN to COL6 and beyond | Keynote lecture by Carsten Bönnemann (National Institutes of Health, USA) at Mitochondrial medicine - therapeutic development 2022. Organised by Wellcome Connecting Science Courses and Conferences #Mitochondria #MitochondrialDisease #MitoMed22 #genomic #genomics
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