5th Symposium Barcelona 2025 - Divesiran from Silence Therapeutics and Q&A
Автор: Global MPN Scientific Foundation
Загружено: 2025-12-10
Просмотров: 11
Silence Therapeutics (Alberto Martínez): Presented their drug divesiran, an RNA-based therapy targeting TMPRSS6 to increase hepcidin and reduce iron availability, aimed at controlling hematocrit and reducing phlebotomy burden in Polycythemia Vera (PV). Shared positive phase I/II data and plans for phase III.
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