After years of uncertainty, Mississippi teen sees drug approval for Barth syndrome
Автор: Roy Howard Community Journalism Center
Загружено: 2025-09-22
Просмотров: 98
Seventeen-year-old Christopher Pena has spent his life battling Barth syndrome, a rare genetic disorder that weakens the body. On Friday, he learned the drug he credits with giving him strength to jump, carry heavy items and keep up in school won accelerated approval from the Food and Drug Administration.
The FDA granted clearance for elamipretide, which will be sold under the brand name Forzinity, as the first treatment for Barth syndrome in patients over 30 kilograms — about 66 pounds.
Read the full story over on our website, https://rhcjcnews.com/5549/news/after....
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