Eye on the Future Forum Fall 2020 Summit

Full recording of the EFF Fall Virtual Summit which took place on September 23, 2020. The focus of this summit is on Leber congenital amaurosis and sepofarsen, the RNA therapy ProQR Therapeutics is developing for LCA10.

Program:

0:00 Welcome to the webinar
Presented by: Daniel de Boer, CEO, ProQR Therapeutics
Daniel de Boer, the CEO of ProQR will open the Fall EFF Summit giving a short introduction of ProQR and the status of ProQR (2:56).
How ProQR has been doing since our EFF conference last February in Paris? How COVID-19 has impacted to our daily work?

6:30 Sepofarsen update
Presented by: Aniz Girach, Chief Medical Officer, ProQR Therapeutics
Aniz Girach will give a short update on the success to date and latest clinical trial findings of the sepofarsen program for CEP290 mediated Leber congenital amaurosis (LCA10) before starting the interactive sessions.

25:23 Live Q&A on LCA and sepofarsen
Dr. Ian M. MacDonald and Dr. Aniz Girach, moderated by Jessica Ibbitson
Immediately after, we will start with a Q&A session with Dr. Ian MacDonald and Dr. Aniz Girach. For 25 minutes they will be answering audience questions about Leber congenital amaurosis 10 and sepofarsen data.

50:43 Panel discussion on patient’s perspective on clinical research
Panelists: Francesca Diodati, Ian MacDonald and Aniz Girach, moderated by Jessica Ibbitson
To finalize the Fall EFF Summit, we would like to give to the audience the chance to ask to our panelists questions about one of the topics of more concern to us: 'patient's perspective on clinical research'. What is their experience on this topic?

1:29:21 Close out
Speaker: Aniz Girach
Thank you and looking forward to the next Eye on the Future Forum event in Spring/Summer 2021. Keep posted on https://www.eyeonthefutureforum.com.

More information on the Illuminate, the sepofarsen clinical trial for LCA10: https://www.lcastudy.com & https://www.proqr.com/illuminate

Music by Scott Holmes