Every Step Matters: How Safety Shapes Our ASO Program Decisions from Discovery to Delivery
Автор: n-Lorem Foundation
Загружено: 2025-11-05
Просмотров: 29
This presentation examines how our rigorous, experience-based process at n-Lorem contributes to our exceptional safety record in the development of individualized ASO medicines. From discovery through treatment and evaluation, safety is not a single checkpoint, it is embedded into every decision we make. We outline the decision-points underpinned by safety considerations across the ASO development pathway and discuss the expertise required to make informed, high-stakes clinical decisions for patients with complex, progressive diseases. This discussion walks through the key considerations for acceptance decisions, identification of the right ASO, and the oversight mechanisms that ensure only the most appropriate therapies move forward, and data exemplifying our experience to date.
Nano-rare Patient Colloquium
October 20, 2025
Sarah Glass, Ph.D.
Chief Operating Officer, n-Lorem
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