Navigating the Complexities of Individualized ASO Development | 2025 Nano-rare Patient Colloquium
Автор: n-Lorem Foundation
Загружено: 2025-11-06
Просмотров: 42
This expert panel examines the central question: Is the n-Lorem process working? Drawing on the themes of safety, oversight, and decision-making introduced in prior talks, panelists explore the nuanced decisions required to ensure safety, optimize clinical outcomes, and responsibly advance individualized therapies for nano-rare patients. The discussion explores real-world outcomes, the scalability of the model, the complexity of treating medically fragile patients, and the standards of evidence required to demonstrate success. Panelists will bring diverse perspectives from clinical practice, regulatory science, and therapeutic development to assess the effectiveness, and future potential, of n-Lorem’s mission.
October 20, 2025
Moderator:
Stanley T. Crooke, M.D., Ph.D.
Founder and CEO, n-Lorem
Panelists:
Julie Douville, Ph.D.
Vice President, ASO Discovery and Development, n-Lorem
Scott Henry, Ph.D.
SVP, Preclinical Development, Ionis Pharmaceuticals
Laurence Mignon, Ph.D.
Executive Director, Clinical Development, n-Lorem
Eugene Schneider, M.D.
Executive Vice President and Chief Clinical Development and Operations Officer, Ionis Pharmaceuticals
Доступные форматы для скачивания:
Скачать видео mp4
-
Информация по загрузке:
