ResearchCon 2022 | Something for Everyone

Genetic therapies can be an intimidating topic, but they will play a critical role in developing treatments for everyone with cystic fibrosis and, one day, a cure. In the closing keynote of ResearchCon 2022, Dr. Manu Jain and Dr. Lynne Quittell, along with an adult with CF, Neema Chandel, provide an overview of genetic therapies, and answers to your top questions.

Originally recorded April 9, 2022.


0:00:00 | Something for Everyone: A look at possibilities and challenges of genetic therapies on the horizon
0:02:13 | Meet Neema Chandel, an adult with cystic fibrosis
0:02:50 | Neema shares her CF story with late diagnosis, transplant, and health disparities
0:08:09 | Introduction to our clinicians, Manu Jain, MD, and Dr. Lynne Quittell, MD
0:08:35 | Manu Jain, MD, provides an update on continuing efforts with genetic therapy
0:12:44 | Differences and similarities between mRNA delivery, gene delivery, and gene editing
0:20:15 | If CFTR were a car: Understanding genetic therapies for CF utilizing the car analogy
0:23:31 | Challenges and timeline to genetic therapies
0:26:35 | Lynne Quittell, MD, provides details on how you can take part in this research
0:32:05 | Learn what’s different about gene therapy trials this time around and how your safety will be protected.
0:36:20 | What are the resources available?
0:38:03 | Lynne Quittell, MD answers your questions
0:40:40 |Shelby Luebbert and Cindy George close out ResearchCon 2022