Pompe Disease and Gene Therapy

Pompe disease

American Society of Gene & Cell Therapy

Gene Therapy

Glycogen

Lysosomes

Автор: ASGCT

Загружено: 18 нояб. 2019 г.

Просмотров: 15 309 просмотров

Описание:

Pompe disease is a genetic disorder that occurs when our bodies lack an important digestive enzyme called acid alpha-glucosidase, or GAA for short. Although gene therapy is not a cure yet, it may offer a one-time treatment to help fight progression of the disease.

The subtitling of these videos was funded in part by a donation from Pfizer, Inc.

Pompe Disease and Gene Therapy

Доступные форматы для скачивания:

Скачать видео mp4

Информация по загрузке:

Скачать аудио mp3

Похожие видео

Hemophilia and Gene Therapy

Hemophilia and Gene Therapy

Pompe Disease (with a mnemonic) -Glycogen Storage Disease Type II (GSD-II) - Biochemistry & Genetics

Pompe Disease (with a mnemonic) -Glycogen Storage Disease Type II (GSD-II) - Biochemistry & Genetics

Горькая правда о жизни 99% людей. Не все готовы услышать это

Горькая правда о жизни 99% людей. Не все готовы услышать это

Viral Vectors Overview

Viral Vectors Overview

Pompe disease - causes, symptoms, diagnosis, treatment, pathology

Pompe disease - causes, symptoms, diagnosis, treatment, pathology

Gene Therapy and Sickle Cell Disease

Gene Therapy and Sickle Cell Disease

The Treatment of Pompe Disease: Clinical Updates in Newborn Screening and Enzyme Replacement

The Treatment of Pompe Disease: Clinical Updates in Newborn Screening and Enzyme Replacement

Gene Therapy Basics (2022 Update)

Gene Therapy Basics (2022 Update)

Советский мультфильм про нашу жизнь !

Советский мультфильм про нашу жизнь !

Danon Disease 101

Danon Disease 101